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BIOENGINEER.ORG
bioengineer.org > gene-therapy-shows-lasting-two-year-gains-in-infants-with-severe-spinal-muscular-atrophy

Gene Therapy Shows Lasting Two-Year Gains in Infants With Severe Spinal

1+ day, 4+ hour ago   (744+ words) A single infusion of a gene therapy delivered within the first months of life continues to transform the course of one of the most devastating neuromuscular diseases of infancy, according to a comprehensive two-year analysis of real-world outcomes drawn from…...